
16 Design & Analysis of Clinical Trials for Economic Evaluation
Process
step
Customer analysis
(epidemiology/
guidelines)
Activity
(+ review/
previous)
Inputs
Ba
launch
Several market
attractiveness
scenarios
Profitability & risk
scenarios
Optimise regional profitability through model
forecost
Forecasts
review with
negotiations
outcomes
Market analysis
(competitive
landscape)
Opportunity
assessment
Initial product
profile
Preliminary test of
value scenarios
with payers and
KOLs
Risk assessment
Profitability
model:
manufacturing
costs analysis and
initial sales &
price scenarios
Efficacy & tolerability +
burden of illness + cost-
efficacy + patient-
reported